Muscular Dystrophy News5h
FDA awards fast track designation to DM1 treatment DYNE-101
The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...
Muscular Dystrophy News2d
Corticosteroid at low dose may help with muscle damage, inflammation
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...
Muscular Dystrophy News6d
Stuck in limbo with both accessible vans out of commission
An accident and a malfunction render both of columnist Betty Vertin's accessible vans useless, leaving the family without transportation.
Muscular Dystrophy News7d
DYNE-101 is leading to functional gains for DM1 patients in trial
The investigational therapy DYNE-101 worked as expected and led to functional improvements for people with myotonic dystrophy type 1 (DM1) in a clinical trial, according to an update from developer ...