RCT-2100 is under development for the treatment of cystic fibrosis (CF). The therapeutic candidate is an mRNA, encoding cystic fibrosis transmembrane conductance regulator (CFTR). It is administered ...
Product approvals in regenerative medicine and rare diseases are among the highlights in our recap of recent FDA regulatory ...
Galicaftor is under clinical development by Sionna Therapeutics and currently in Phase II for Cystic Fibrosis.
As Vertex Pharmaceuticals reels from a painful trial readout for its pain candidate suzetrigine, the Boston biotech has ...
The agency’s main drug review office cleared 50 novel medicines last year, short of 2018’s record total but on the higher end ...
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According to Vertex Pharmaceuticals, approximately 300 additional people with CF are now eligible to receive treatment.
What's better than one dual meet? Two, of course. General McLane wrestling hosted the Corry boys and girls for a doubleheader Thursday on "Takedown Cystic Fibrosis" night.
A new charity football team in Peterborough has been set up to honour the memory of Jordan Smith and raise awareness of ...